University of Michigan scientists running a human trial of the first ever gene therapy treatment for pain relief say that the virus-based vector which triggers the expression of a naturally occurring opioid appears to provide substantial pain relief. Their study, published in the Annals of Neurology, used a novel human-grade vector agent known as NP2. […]
Tag Archives | gene therapy
New Delivery Method For Gene Therapy
Gene therapy theoretically makes it possible to introduce genes into cells to cure disease or address deficiencies in biological processes. But in order for gene therapy to work, foreign (or synthetic) DNA must be introduced into host cells, which is a non-trivial task. Traditionally, researchers inserted foreign DNA through the cell membrane which had been […]
Three (No Longer) Blind Mice
Gene therapy has been successfully used to restore sight in mice with a form of hereditary blindness; possibly leading to new treatments for common blinding diseases. Writing about their work in Nature Medicine, the University of Florida (UF) scientists described how they used a harmless virus to deliver corrective genes to mice with a genetic […]